UMDF Connect

UMDF Joins Other Mito Advocacy Groups to Issue Statement and Call to Action Regarding the FDA’s DCA Denial

Sep 4, 2025 | Awareness, Mito Advocacy, Press Room

Sept. 4, 2025 -- Earlier today, Saol Therapeutics shared the U.S. Food and Drug Administration (FDA) has issued a Complete Response Letter (CRL) regarding the company’s application for dichloroacetate (DCA) to treat Pyruvate Dehydrogenase Complex Deficiency...

August 2025 Newsletter: No-Cost Genetic Testing, World Mito Week, FDA Action, Ask the Mito Doc Returns, and more

Aug 12, 2025 | Press Room, UMDF Connect Newsletter

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Energize the Fight – World Mitochondrial Disease Week 2025

Aug 8, 2025 | Awareness, Press Room

We’re excited to unite with other mitochondrial disease-focused patient advocacy groups across the globe to spread awareness on World Mitochondrial Disease Week, Monday, Sept. 15 to Sunday, Sept. 21 ! Together, we can promote understanding and recognition with the...

Advocacy Action: Ask FDA to Reconsider Elamipretide Decision

Aug 6, 2025 | Mito Advocacy, Press Room

Barth Syndrome Foundation, UMDF, and MitoAction leadership were recently notified by Stealth BioTherapeutics that FDA has refused their request to reconsider the elamipretide new drug application (NDA). This refusal to reconsider comes despite a positive Type A...

July 2025 Newsletter: Mito Fund Invests in POLG-Focused Company, MitoMed Grant & Award Winners, mitoSHARE Studies, and more

Jul 2, 2025 | Press Room, UMDF Connect Newsletter

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Ask the Mito Doc – May 2025; Q&A

May 15, 2025 | Ask the Mito Doc

Ask the Mito Doc - May 2025 Q&A All answers today are based on personal experience of the participants. As always, please consult your personal physician prior to taking any action.Ask the Mito Doc - May 2025: Mitochondrial Disease and Biorepositories - Why...

UMDF Cosigns Letter to HHS Urging Preservation of Federal Newborn Screening System

May 5, 2025 | Mito Advocacy, Press Room

Ask the Mito Doc – April 2025; Q&A

Apr 30, 2025 | Ask the Mito Doc

Ask the Mito Doc - April 2025 Q&A All answers today are based on personal experience of the participants. As always, please consult your personal physician prior to taking any action.Ask the Mito Doc - April 2025: Integrating Physical and Emotional Pain...