UMDF Connect
Advocacy Action: Ask FDA to Reconsider Elamipretide Decision
Barth Syndrome Foundation, UMDF, and MitoAction leadership were recently notified by Stealth BioTherapeutics that FDA has refused their request to reconsider the elamipretide new drug application (NDA). This refusal to reconsider comes despite a positive Type A...
July 2025 Newsletter: Mito Fund Invests in POLG-Focused Company, MitoMed Grant & Award Winners, mitoSHARE Studies, and more
Signup to receive the UMDF newsletter in your email monthly at umdf.org/newsletter-signup.
Ask the Mito Doc – May 2025; Q&A
Ask the Mito Doc - May 2025 Q&A All answers today are based on personal experience of the participants. As always, please consult your personal physician prior to taking any action.Ask the Mito Doc - May 2025: Mitochondrial Disease and Biorepositories - Why...
UMDF Cosigns Letter to HHS Urging Preservation of Federal Newborn Screening System
Ask the Mito Doc – April 2025; Q&A
Ask the Mito Doc - April 2025 Q&A All answers today are based on personal experience of the participants. As always, please consult your personal physician prior to taking any action.Ask the Mito Doc - April 2025: Integrating Physical and Emotional Pain...
Ask Your House Representative to Support Mito Research Funding in 2026 Appropriations
April 2025 Newsletter: New Mito Biorepository, MitoMed Highlights, Medicaid Survey Results, and More
Signup to receive the UMDF newsletter in your email monthly at umdf.org/newsletter-signup.
UMDF Partners with COMBINEDBrain to Develop a Mitochondrial Disease Biorepository
UMDF has partnered with the nonprofit COMBINEDBrain to develop a mitochondrial disease biorepository hosted on mitoSHARE, UMDF's patient registry. Patients with any form of a genetically confirmed mitochondrial disease can now participate in the biorepository by...
UMDF Cosigns Letter to Congressional Leaders Supporting Accelerating Kids’ Access to Care Act
Ask the Mito Doc – March 2025; Q&A
Ask the Mito Doc - March 2025 Q&A All answers today are based on personal experience of the participants. As always, please consult your personal physician prior to taking any action.Ask the Mito Doc - March 2025: Clinical Trial Readiness & Clinical...