The “Voice of the Patient” Report
The Externally-led Patient-Focused Drug Development meeting focusing on mitochondrial disease was held on March 29, 2019. We are thankful for all the patients and caregivers who contributed their time and effort into making the meeting a success.
The “Voice of the Patient” report resulting from the meeting was reviewed and approved by the Food and Drug Administration (FDA). A video of the entire meeting is also embedded below as well as links for supplementary resource materials. We encourage you to download, read and share all of these materials.
Additional mechanisms for capturing the mitochondrial disease patient perspective are in development.
Voice of the Patient
Download the Voice of the Patient Report, a summary report of the Externally-led Patient-Focused Drug Development (PFDD) meeting and an account of the perspectives of patients and caregivers who participated.
Mitochondrial Disease Externally-led Patient-Focused Drug Development Meeting
Presented March 29, 2019
Meeting Program
Download a copy of the meeting program, including biographies of our speakers and panel members.
Meeting Transcript
Download a copy of the meeting transcript.