UMDF Partners with MDA to Co-Fund Two New Mito Research Grants
UMDF has teamed up with the Muscular Dystrophy Association (MDA) to co-fund two new research projects to accelerate the development of...
Read moreLatest News -Awareness
FDA Approves First-Ever TK2d Therapy
11/3/25, 5pm EST — Earlier today, the U.S. Food and Drug Administration (FDA) approved UCB’s Kygevvi (doxecitine and doxribtimine) to...
Read moreSPECIAL NATIONAL AUTHOR’S DAY FEATURE: Mito Patient and His Mom Talk About Self-Publishing “Children’s Chapter Adventure” Book
KSS Patient and Mom Talk About Self-Publishing Their “Children’s Chapter Adventure” Book Thomas Gordon is not your typical...
Read morePRESS RELEASE: Leading Clinicians and Researchers Urge FDA to Reconsider Path Forward for DCA in Pyruvate Dehydrogenase Complex Deficiency
Leading advocacy groups and more than 80 scientific and medical leaders call on FDA to act urgently on DCA approval for PDCD, a rare and...
Read moreREAD THE LETTER: Leading Clinicians and Researchers Urge FDA to Reconsider Path Forward for DCA in Pyruvate Dehydrogenase Complex Deficiency
Click the Expand Button in the bottom right on the widget for a larger, full-screen view of the...
Read moreFDA Approves First Mitochondrial Disease Therapy: Stealth BioTherapeutics’ Elamipretide for Barth Syndrome
UMDF celebrates historic milestone for rare disease community The United Mitochondrial Disease Foundation (UMDF), the largest mitochondrial...
Read moreA Special World Mitochondrial Disease Week Message from UMDF President & CEO Kristen Clifford
Today marks the official kickoff of World Mitochondrial Disease Week, a time designed to help the public better understand mitochondrial...
Read moreUMDF Joins Other Mito Advocacy Groups to Issue Statement and Call to Action Regarding the FDA’s DCA Denial
Sept. 4, 2025 — Earlier today, Saol Therapeutics shared the U.S. Food and Drug Administration (FDA) has issued a Complete Response...
Read moreEnergize the Fight – World Mitochondrial Disease Week 2025
We’re excited to unite with other mitochondrial disease-focused patient advocacy groups across the globe to spread awareness on World...
Read moreUMDF Partners with COMBINEDBrain to Develop a Mitochondrial Disease Biorepository
UMDF has partnered with the nonprofit COMBINEDBrain to develop a mitochondrial disease biorepository hosted on mitoSHARE, UMDF’s patient...
Read more