Signup to receive the UMDF newsletter in your email monthly at umdf.org/newsletter-signup. FDA Approves First-Ever TK2d Therapy Earlier this...
Read more11/3/25, 5pm EST — Earlier today, the U.S. Food and Drug Administration (FDA) approved UCB’s Kygevvi (doxecitine and doxribtimine) to...
Read moreKSS Patient and Mom Talk About Self-Publishing Their “Children’s Chapter Adventure” Book Thomas Gordon is not your typical...
Read moreLeading advocacy groups and more than 80 scientific and medical leaders call on FDA to act urgently on DCA approval for PDCD, a rare and...
Read moreSignup to receive the UMDF newsletter in your email monthly at umdf.org/newsletter-signup. FDA Announces First Approved Mito Therapy: Forzinity...
Read moreUMDF celebrates historic milestone for rare disease community The United Mitochondrial Disease Foundation (UMDF), the largest mitochondrial...
Read moreToday marks the official kickoff of World Mitochondrial Disease Week, a time designed to help the public better understand mitochondrial...
Read moreSignup to receive the UMDF newsletter in your email monthly at umdf.org/newsletter-signup. UMDF Preps for Mitochondrial Disease Awareness Week...
Read moreSept. 4, 2025 — Earlier today, Saol Therapeutics shared the U.S. Food and Drug Administration (FDA) has issued a Complete Response...
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