FDA Advisory Committee Deems Potential Barth Syndrome Drug “Effective” Earlier this month, an FDA Advisory Committee voted 10-6...
Read: Advocacy Update – Oct 2024: FDA AdComm Brings Good News, Plus DC End of Year BusinessAfter a full day of testimony that consistently demonstrated the need and efficacy of elamipretide for the treatment of Barth Syndrome, an FDA...
Read: UMDF Reacts to FDA Advisory Committee’s Elamipretide RecommendationRead UMDF’s Comment to FDA’s Advisory Committee regarding New Drug Application for Elamipretide in Barth...
Read: UMDF’s Comment to FDA’s Advisory Committee Regarding ElamipretideThe United Mitochondrial Disease Foundation today announced a new $100,000 grant to Madhurima Saha, PhD, of the University of Florida, for...
Read: UMDF Announces $100k Award for MEPAN Research, Bringing Total Research Grants Awarded to More Than $1 Million in the Last YearUMDF Co-Signs Letter Supporting Rare Pediatric Disease Priority Review Voucher...
Read: Advocacy Update – UMDF Co-Signs Letter Supporting PRV ReauthorizationThis coming week, September 16 – 22, 2024, marks World Mitochondrial Disease Week. For me, the week is deeply personal. This year marks twenty...
Read: A special message from UMDF for World Mitochondrial Disease Week 2024In a few weeks, we’ll join other mitochondrial disease-focused patient advocacy groups across the globe in marking World Mitochondrial Disease...
Read: Advocacy Update – Aug 2024: Help Shape the Legislative Landscape for the Mito Community Through Survey, UMDF Action ItemsOn the heels of our traditional research grant funding cycle culminating at UMDF’s annual Mitochondrial Medicine conference this past June, the...
Read: UMDF Announces Two New Postdoctoral Fellowship Research GrantsUMDF Issues Response to Congressional 21st Century Cures Act RFI DOWNLOAD this document (PDF)...
Read: UMDF Issues Response to Congressional 21st Century Cures Act RFI